New drug trial targets debilitating itching in rare liver disease

NCT ID NCT05543174

Summary

This study tested whether the drug TAK-625 could help people with Alagille Syndrome, a rare genetic disorder that causes severe liver problems and intense itching. Seven Japanese participants, including infants and children, received the drug for up to 34 months to see if it safely lowered harmful bile acids in their blood and reduced their itching. The goal was to find the right dose to better manage this lifelong condition.

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Contacts and locations

Locations

  • Juntendo University Hospital

    Bunkyo-ku, Tokyo, Japan

  • Kindai University Nara Hospital

    Ikoma, Nara, Japan

  • Kyoto University Hospital

    Kyoto, Japan

  • Miyagi Children's Hospital

    Sendai, Miyagi, Japan

  • Osaka University Hospital

    Suita, Osaka, Japan

  • Saitama Prefectural Children's Medical Center

    Saitama, Japan

  • University of Tsukuba Hospital

    Tsukuba, Ibaraki, Japan

  • Yokohamashi Tobu Hospital

    Yokohama, Kanagawa, Japan

Conditions

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