New drug aims to control rare blood disorders without lifelong steroids
NCT ID NCT07104565
First seen Jun 27, 2026 · Last updated Aug 07, 2026 · Updated 8 times
Summary
This study tests a drug called tafasitamab in adults with two rare autoimmune blood disorders: immune thrombocytopenia (ITP) and warm autoimmune hemolytic anemia (wAIHA). The goal is to see if it can safely raise blood cell counts and reduce the need for other treatments. About 56 participants will receive the drug and be monitored for up to 48 weeks.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Email: •••••@•••••
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Contact
Email: •••••@•••••
Locations
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Amsterdam Umc, Locatie Vumc
RECRUITINGAmsterdam, 1105 AZ, Netherlands
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Azienda Ospedale Universita Di Padova
RECRUITINGPadova, 35128, Italy
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Azienda Ospedaliera Universitaria Federico Ii
RECRUITINGNaples, 80131, Italy
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Azienda Ospedaliero-Universitaria Orsola-Malpighi - Universita Degli Studi Di Bologna
RECRUITINGBologna, 40138, Italy
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Azienda Socio Sanitaria Territoriale Degli Spedali Civili Di Brescia (Presidio Montichiari)
RECRUITINGBrescia, 25123, Italy
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Barts Hospital
RECRUITINGLondon, E1 2ES, United Kingdom
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Beth Israel Deaconess Medical Center
RECRUITINGBoston, Massachusetts, 02215, United States
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Box Hill Hospital
RECRUITINGBox Hill, Victoria, 03128, Australia
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Castle Hill Hospital
RECRUITINGCottingham, HU16 5JQ, United Kingdom
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Chru de Nancy- Hopital de Brabois
RECRUITINGVandœuvre-lès-Nancy, 54500, France
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Chu Angers - Hôpital Hôtel Dieu
RECRUITINGAngers, 49933, France
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Chu Bordeaux - Hôpital Haut-Lévêque
RECRUITINGPessac, 33604, France
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Chu Caen - Hôpital de La Côte de Nacre
RECRUITINGCaen, 14033, France
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Chu Dijon - Hopital Du Bocage
RECRUITINGDijon, 21079, France
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Erasmus Medisch Centrum
RECRUITINGRotterdam, 3015 GD, Netherlands
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Fondazione Irccs Ca' Granda - Ospedale Maggiore Policlinico
RECRUITINGMilan, 20122, Italy
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Fondazione Policlinico Universitario Agostino Gemelli Irccs
RECRUITINGRoma, 00136, Italy
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Fred Hutchinson Cancer Center
NOT_YET_RECRUITINGSeattle, Washington, 98109, United States
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Gnp Research
RECRUITINGCooper City, Florida, 33024, United States
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Hopital Purpan
RECRUITINGToulouse, 31059, France
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Hospital Universitario La Paz
RECRUITINGMadrid, 28046, Spain
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Hôpital Henri Mondor
RECRUITINGCréteil, 94010, France
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Ico Badalona. Hospital Universitario Germans Trias I Pujol
RECRUITINGBadalona, 08916, Spain
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Inova Schar Cancer Institute
RECRUITINGFairfax, Virginia, 22031, United States
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Istituto Romagnolo Per Lo Studio Dei Tumori Dino Amadori
RECRUITINGMeldola, 47014, Italy
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Monash Medical Centre Clayton
RECRUITINGClayton, Victoria, 03168, Australia
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Montefiore Medical Center
RECRUITINGThe Bronx, New York, 10461, United States
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Ospedale San Raffaele
RECRUITINGMilan, 20132, Italy
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Palo Verde Cancer Specialists Palo Verde Hematology Oncology, Ltd Glendale
RECRUITINGGlendale, Arizona, 85304, United States
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Plymouth Hospitals Nhs Trust
RECRUITINGPlymouth, PL6 8DH, United Kingdom
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Princess Alexandra Hospital Australia
RECRUITINGWoolloongabba, Queensland, 04102, Australia
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Radboudumc
RECRUITINGNijmegen, 6500 HB, Netherlands
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Rocky Mountain Cancer Centers
RECRUITINGLone Tree, Colorado, 80124, United States
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St Vincent'S Hospital Sydney
RECRUITINGDarlinghurst, New South Wales, 02010, Australia
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The Alfred Hospital
RECRUITINGMelbourne, Victoria, 03004, Australia
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Townsville University Hospital
RECRUITINGDouglas, Queensland, 04814, Australia
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University Medical Center Utrecht
RECRUITINGUtrecht, 3584 CX, Netherlands
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Usc Norris Comprehensive Cancer Center
RECRUITINGLos Angeles, California, 90033, United States
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Versiti Bloodcenter of Wisconsin Bcw Milwaukee
NOT_YET_RECRUITINGMilwaukee, Wisconsin, 53233, United States
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Yale University School of Medicine
NOT_YET_RECRUITINGNew Haven, Connecticut, 06510-3221, United States
More trials for these conditions
Other studies related to the condition(s) this trial covers.
- Can a new drug calm the immune System's attack on blood cells?
- Experimental injection aims to boost platelets in chronic blood disorder
- New combo therapy aims to boost platelets in immune disorder
- Double attack on blood disorder: could two drugs beat one for stubborn ITP?
- Could a cholesterol drug and antioxidant help treat a rare bleeding disorder?
- New hope for lupus patients with dangerous low platelet counts