New stem cell approach aims to fix broken immune systems

NCT ID NCT04232085

First seen Jan 04, 2026 · Last updated May 15, 2026 · Updated 19 times

Summary

This study tests a stem cell transplant method for people with serious immune disorders or bone marrow failure. The goal is to see if a gentler pre-transplant treatment, followed by a drug to prevent rejection, can help donor cells take over and restore healthy blood and immune function. About 27 participants will be followed for at least a year to check if the transplant works and how safe it is.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Johns Hopkins University

    RECRUITING

    Baltimore, Maryland, 21287, United States

    Contact

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.