New hope for rare immune disorder: can a transplant reset the Body's defenses?
NCT ID NCT01861106
Summary
This study is testing whether a stem cell transplant from a matched donor can treat GATA2 deficiency, a rare genetic disorder that causes serious infections and can lead to blood cancers. The transplant aims to replace the patient's faulty bone marrow with healthy donor cells to restore normal blood and immune system function. The trial is enrolling 144 participants aged 6 to 70 who have this condition and a suitable donor.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Conditions
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