Life-Saving transplant trial offers cure for devastating genetic immune disease
NCT ID NCT01176006
Summary
This study is testing a stem cell transplant as a potential cure for DOCK8 deficiency, a rare genetic disorder that severely weakens the immune system. The trial is enrolling patients aged 4-35 who have suffered life-threatening infections and have a matched donor. Researchers are evaluating transplants from siblings, unrelated donors, or partially matched family members to see if they can rebuild a healthy immune system.
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Contacts and locations
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Locations
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National Institutes of Health Clinical Center
Bethesda, Maryland, 20892, United States
Conditions
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