Could an amino acid shorten sickle cell pain crises?

NCT ID NCT04839354

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This phase 3 trial tests whether intravenous arginine, an amino acid, can shorten painful episodes in children with sickle cell disease. Participants aged 3 to 21 receive either arginine or a placebo alongside standard pain treatment. The study measures how quickly the crisis resolves and how much opioid pain medication is needed.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

L-arginine hydrochloride

What this could lead to

If it works, this could provide a new, safer way to shorten painful sickle cell crises and reduce reliance on opioids for children.

What could go wrong

This is an early-phase trial, and arginine may not prove more effective than placebo. Potential side effects include allergic reactions or metabolic imbalances.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

agnosia sickle cell disease

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Children's Healthcare of Atlanta at Egleston

    Atlanta, Georgia, 30322, United States

  • Children's Healthcare of Atlanta at Hughes Spalding

    Atlanta, Georgia, 03322, United States

  • Children's Hospital Los Angeles

    Los Angeles, California, 90027, United States

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

  • Children's National Medical Center

    Washington D.C., District of Columbia, 20010, United States

  • Medical College of Wisconsin/Wisconsin Children's Hospital

    Wauwatosa, Wisconsin, 53226, United States

  • Nationwide Children's Hospital

    Columbus, Ohio, 43205, United States

  • Texas Children's Hospital/Baylor College of Medicine

    Houston, Texas, 77030, United States

  • UCSF Benioff Children's Hospital

    San Francisco, California, 94158, United States

  • Washington University/St. Louis Children's Hospital

    St Louis, Missouri, 63110, United States