Hope for rare skin disease: new drug trial shows promise

NCT ID NCT05856526

First seen Nov 01, 2025 · Last updated Apr 28, 2026 · Updated 31 times

Summary

This study tested a medicine called spesolimab in people aged 12 and older with Netherton syndrome, a rare genetic skin condition causing redness and scaling. Participants received either spesolimab or a placebo injection, with the placebo group switching to the real drug after 4 months. The goal was to see if spesolimab could reduce skin symptoms, but the study was ended early.

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Contacts and locations

Locations

  • ASMC-IPSMC-skin and Veneral Diseases

    Sofia, 1407, Bulgaria

  • Azienda Ospedaliera Universitaria Citta Della Salute E Della Scienza Di Torino

    Torino, 10126, Italy

  • Beijing Children's Hospital, Capital Medical University

    Beijing, 100045, China

  • Dermatology Hospital, Chinese Academy of Medical Sciences

    Nanjing, 210000, China

  • Erasmus MC Sophia Kinderziekenhuis

    Rotterdam, 3015 GD, Netherlands

  • HOP Saint-Louis

    Paris, 75010, France

  • Hospital Tunku Azizah

    Kuala Lumpur, 50300, Malaysia

  • Istituto Dermopatico Dell'Immacolata - IDI - IRCCS

    Roma, 00167, Italy

  • Juntendo University Urayasu Hospital

    Chiba, Urayasu, 279-0021, Japan

  • Klinikum der Universität München AÖR

    München, 80337, Germany

  • Medical University of South Carolina

    Charleston, South Carolina, 29425, United States

  • Mission Dermatology Center

    Rancho Santa Margarita, California, 92688, United States

  • Nagoya University Hospital

    Aichi, Nagoya, 466-8560, Japan

  • Okayama University Hospital

    Okayama, Okayama, 700-8558, Japan

  • Queen Elizabeth University Hospital

    Glasgow, G51 4TF, United Kingdom

  • Shanghai Skin Disease Hospital

    Shanghai, 200000, China

  • Sourasky Medical Center

    Tel Aviv, 6423906, Israel

  • Southern Medical University Dermatology Hospital

    Guangzhou, 510091, China

  • The Children's Hospital Zhejiang University School Of Medicine

    Hangzhou, 310000, China

  • The First Affiliated Hospital, Zhejiang University

    Hangzhou, 310003, China

  • ULS de São José, E.P.E. - Hospital Sto. António Capuchos

    Lisbon, 1169-050, Portugal

  • University Children Hospital Zürich

    Zurich, 8032, Switzerland

  • Universitätsklinikum Heidelberg

    Heidelberg, 69120, Germany

  • Universitätsklinikum Schleswig-Holstein, Campus Kiel

    Kiel, 24105, Germany

  • Virginia Clinical Research, Inc.

    Norfolk, Virginia, 23502, United States

  • Westmead Hospital

    Westmead, New South Wales, 2145, Australia

  • Xinhua Hospital Affiliated to Shanghai Jiaotong University

    Shanghai, 200092, China

  • Yale University School of Medicine

    New Haven, Connecticut, 06519, United States

Conditions

Explore the condition pages connected to this study.