New hope for sickle cell cure: drug may prevent transplant failure

NCT ID NCT07252050

Summary

This study is testing if adding a drug called ruxolitinib to a stem cell transplant can help prevent the body from rejecting the new cells, which is a major risk. It aims to improve the chance of a cure for children and young adults with severe sickle cell disease. Up to 24 participants will receive the new drug combination and be followed for two years after their transplant.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Healthcare of Atlanta

    Atlanta, Georgia, 30329, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Hospital of Colorado

    Aurora, Colorado, 80045, United States

    Contact

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

    Contact

  • Manning Family Children's

    New Orleans, Louisiana, 70118, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.