New drug aimed at making risky sickle cell cure more reliable

NCT ID NCT07252050

Summary

This study is testing if adding a drug called ruxolitinib to a stem cell transplant can make the procedure more successful for children and young adults with severe sickle cell disease. The main goal is to reduce the chance of the body rejecting the new cells (graft failure), which can cause the disease to return. Up to 24 participants will receive the treatment and be followed for two years to see if it improves survival without graft failure.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Healthcare of Atlanta

    Atlanta, Georgia, 30329, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Hospital of Colorado

    Aurora, Colorado, 80045, United States

    Contact

  • Children's Hospital of Philadelphia

    Philadelphia, Pennsylvania, 19104, United States

    Contact

  • Manning Family Children's

    New Orleans, Louisiana, 70118, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.