First step toward gene therapy for rare bleeding disorder?
NCT ID NCT06414889
First seen Jan 05, 2026 · Last updated Jun 15, 2026 · Updated 30 times
Summary
This study is for people with RUNX1 familial platelet disorder, a rare inherited condition that raises the risk of bleeding and leukemia. Researchers want to see if it's safe to collect the person's own blood stem cells using a standard process. Only 4 participants will take part in this early-phase trial at MD Anderson Cancer Center.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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MD Anderson Cancer Center
RECRUITINGHouston, Texas, 77030, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Conditions
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