New hope for controlling a rare blood disorder that raises cancer risk
NCT ID NCT06261060
Summary
This study is testing if a low dose of the drug sirolimus is safe and can improve blood cell production in adults with RUNX1 familial platelet disorder. This inherited condition causes low platelets, easy bleeding, and a high risk of blood cancers. Researchers will see if the drug can increase platelet counts and improve other blood cell functions over a treatment period.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
Get updates
Get notified about this study
Sign up to get updates when this study changes or when new studies for FAMILIAL PLATELET DISORDER are added.
By submitting, you agree to our Terms of use
Contacts and locations
Show contact details
Enter your email to view the contact information for this study.
By submitting, you agree to our Terms of use
Study contacts
-
Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
-
MD Anderson Cancer Center
RECRUITINGHouston, Texas, 77030, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact
Conditions
Explore the condition pages connected to this study.