New hope for controlling a rare blood disorder that raises cancer risk

NCT ID NCT06261060

Summary

This study is testing if a low dose of the drug sirolimus is safe and can improve blood cell production in adults with RUNX1 familial platelet disorder. This inherited condition causes low platelets, easy bleeding, and a high risk of blood cancers. Researchers will see if the drug can increase platelet counts and improve other blood cell functions over a treatment period.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • MD Anderson Cancer Center

    RECRUITING

    Houston, Texas, 77030, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

Conditions

Explore the condition pages connected to this study.