Experimental drug for rare bone marrow disease shows early promise, but study halted

NCT ID NCT04409080

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study tested an experimental drug called REGN7257 in 17 people with severe aplastic anemia, a rare condition where the bone marrow stops making enough blood cells. The drug was given to patients whose disease did not get better or came back after standard immune-suppressing treatments. The main goal was to check safety and see if the drug could improve blood cell counts, but the study was stopped early.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

acquired aplastic anemia aplastic anemia Recurrence

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Cleveland Clinic Foundation

    Cleveland, Ohio, 44195, United States

  • Ewha Womans University Medical Centre

    Seoul, Seoul Capital Area, 07985, South Korea

  • Gachon University Gil Hospital

    Incheon, Gyeonggi-do, 21565, South Korea

  • Hopital Saint-Louis - APHP

    Paris, Île-de-France Region, 75010, France

  • King's College Hospital, London

    London, SE5 9RS, United Kingdom

  • Samsung Medical Center

    Seoul, Seoul Capital Area, 06351, South Korea

  • Seoul National University Hospital

    Seoul, Seoul Capital Area, 03080, South Korea

  • St James's University Hospital

    Leeds, West Yorkshire, LS97TF, United Kingdom

  • The Catholic University of Korea, Seoul St. Marys Hospital

    Seoul, Seoul Capital Area, 06591, South Korea

  • The University of Texas MD Anderson Cancer Center

    Houston, Texas, 77030, United States