New hope for duchenne boys: experimental drug RAG-18 enters human testing

NCT ID NCT07282652

First seen Dec 26, 2025 · Last updated May 15, 2026 · Updated 21 times

Summary

This early-stage study tests the safety of a new drug, RAG-18, in 12 boys aged 4-15 with Duchenne muscular dystrophy. The drug is given through a vein, and researchers will check for side effects, how the body processes the drug, and whether it helps slow muscle damage. The goal is to find a safe dose for future studies.

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Contacts and locations

Locations

  • Peking Union Medical College Hospital

    Beijing, 100730, China

Conditions

Explore the condition pages connected to this study.