Hope for tots with rare gut disease in new drug trial
NCT ID NCT07142343
Summary
This study is checking the safety of an experimental drug called pozelimab in young children (ages 1-5) with a very rare and serious genetic condition called CHAPLE disease. CHAPLE can cause life-threatening stomach and heart problems. Researchers will closely monitor the children for side effects and see how the drug affects their blood protein levels.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Marmara University Hospital
RECRUITINGIstanbul, 10 34899, Turkey (Türkiye)
Conditions
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