Could Off-Label drugs help cystic fibrosis patients with rare gene changes?
NCT ID NCT03587961
First seen Nov 01, 2025 · Last updated May 10, 2026 · Updated 33 times
Summary
This study tests whether certain CF drugs, already approved for some people with cystic fibrosis, can help those with less common CFTR gene mutations. About 20 participants aged 6 and older will try these off-label medications to see if their lung function improves. The goal is to find personalized treatment options for people whose mutations are not currently covered by approved therapies.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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University of Alabama at Birmingham
RECRUITINGBirmingham, Alabama, 35233, United States
Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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