New hope for kids with rare blood disorder: early drug test aims to boost treatment success

NCT ID NCT06430788

Summary

This study is testing if giving a drug called emapalumab right after diagnosis can help children and young adults with severe aplastic anemia. Aplastic anemia is a rare condition where the bone marrow stops making enough blood cells. Researchers want to see if adding emapalumab early makes standard treatments work better and helps patients' blood counts recover faster.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Children's Hospital of Philadelphia (Data Collection AND Specimen Analysis)

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

    Contact Phone: •••-•••-••••

  • Children's Hospital of Wisconsin (Data Collection Only)

    RECRUITING

    Milwaukee, Wisconsin, 53226, United States

    Contact Phone: •••-•••-••••

  • Cincinnati Children's Hospital Medical Center (Data collection only)

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Medical College of Wisconsin (Data Collection AND Data Analysis)

    NOT_YET_RECRUITING

    Milwaukee, Wisconsin, 53226, United States

    Contact Phone: •••-•••-••••

  • Memorial Sloan Kettering Cancer Center (All Protocol Activities)

    RECRUITING

    New York, New York, 10065, United States

    Contact Phone: •••-•••-••••

  • Virginia Commonwealth University (Data Collection Only )

    RECRUITING

    Richmond, Virginia, 23219, United States

    Contact Phone: •••-•••-••••

Conditions

Explore the condition pages connected to this study.