New hope for rare leukemia: oral drug shows promise in early trial

NCT ID NCT05141682

First seen Nov 10, 2025 · Last updated Jun 21, 2026 · Updated 35 times

Summary

This phase I/II trial tests an oral chemotherapy drug called azacitidine (CC-486) in 11 adults with a rare type of leukemia (T-LGLL) that has come back or not responded to prior treatment. The study aims to find the best dose and see if the drug can shrink or control the cancer. Researchers will also track how long any response lasts and monitor side effects.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Ohio State University Comprehensive Cancer Center

    Columbus, Ohio, 43210, United States

  • University of Virginia

    Charlottesville, Virginia, 22908, United States

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

oral azacitidine (CC-486)

What this could lead to

If it works, this could offer a new treatment option for patients with T-LGLL leukemia that has not responded to standard therapies.

What could go wrong

This is a small, early-phase trial with only 11 participants, so results may not apply broadly. The drug may cause side effects or fail to control the disease.

Conditions

The condition(s) this trial relates to.

Leukemia, Large Granular Lymphocytic T-cell large granular lymphocyte leukemia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.