Risdiplam's hidden benefit: fixing Nerve-Muscle links in SMA
NCT ID NCT05219487
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study looked at 18 adults with spinal muscular atrophy (SMA) who had taken the oral medication risdiplam for at least one year. Researchers measured how well nerves and muscles communicate by using electrical stimulation tests. The goal was to see if risdiplam improves these connections compared to historical data. This was an observational study, meaning participants received their usual treatment, and no new drugs were tested.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
Locations
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The Ohio State University Wexner Medical Center
Columbus, Ohio, 43210, United States
More trials for these conditions
Other studies related to the condition(s) this trial covers.
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- Higher dose of spinraza tested in SMA patients who already tried risdiplam