Scientists probe how SMA drug affects nerve signals
Knowledge-focused
Completed
This study aimed to understand how the approved drug Risdiplam affects the connection between nerves and muscles in adults with Spinal Muscular Atrophy (SMA). It observed 18 adults who had already been taking the daily oral medication for at least one year. Researchers performed …
Sponsor: Bakri Elsheikh • Aim: Knowledge-focused
Last updated Mar 17, 2026 13:09 UTC