Immunotherapy duo tackles rare nerve cancer in early trial

NCT ID NCT04465643

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 2 times

Summary

This early-phase trial tested whether giving two immunotherapy drugs (nivolumab and ipilimumab) before standard surgery, chemotherapy, or radiation is safe and feasible for people with Neurofibromatosis Type 1 who have a rare malignant peripheral nerve sheath tumor. Only 13 participants were enrolled. The main goals were to check for side effects and see if the drugs could be given without delaying standard treatment. The study does not yet prove whether this combination helps shrink tumors or improves survival.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

nivolumab and ipilimumab (immunotherapy drugs)

What this could lead to

If this approach proves safe and feasible, it could lead to larger studies testing whether these drugs can shrink tumors before surgery and improve outcomes for people with this rare nerve cancer.

What could go wrong

This is a very small, early-phase trial with only 13 participants, so results may not apply to everyone. The drugs can cause serious immune-related side effects, and it is not yet known if they actually help control the tumor long-term.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

malignant peripheral nerve sheath tumor nerve sheath neoplasm peripheral nervous system neoplasm

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Johns Hopkins Medical Institution

    Baltimore, Maryland, 21287, United States