Sprinkle of hope: new formulation tested for Toddlers' tumors

NCT ID NCT05309668

Summary

This study is testing a new 'sprinkle' granule form of a drug called selumetinib for very young children (ages 1 to 7) with neurofibromatosis type 1 (NF1) who have painful or problematic tumors that cannot be removed by surgery. The main goals are to find the right dose for this age group, understand how the body processes the drug, and check its safety. Researchers will also look for early signs that the treatment might help shrink these tumors.

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Contacts and locations

Locations

  • Research Site

    Akron, Ohio, 44308, United States

  • Research Site

    Philadelphia, Pennsylvania, 19104, United States

  • Research Site

    Houston, Texas, 77030, United States

  • Research Site

    Richmond, Virginia, 23219, United States

  • Research Site

    Hamburg, 20246, Germany

  • Research Site

    München, 80337, Germany

  • Research Site

    Tübingen, 72076, Germany

  • Research Site

    Milan, 20133, Italy

  • Research Site

    Rome, 00165, Italy

  • Research Site

    Nagoya, 466-8560, Japan

  • Research Site

    Setagaya City, 157-8535, Japan

  • Research Site

    Rotterdam, 3015 GD, Netherlands

  • Research Site

    Moscow, 119620, Russia

  • Research Site

    Moscow, 125412, Russia

  • Research Site

    Barcelona, 08950, Spain

  • Research Site

    Madrid, Spain

Conditions

Explore the condition pages connected to this study.