MRNA 'Repair' for immune cells shows promise in rare infection disease

NCT ID NCT05189925

First seen Nov 01, 2025 · Last updated May 14, 2026 · Updated 29 times

Summary

This early-stage study tests a new approach for chronic granulomatous disease (CGD), a genetic condition that leaves people unable to fight off infections. Researchers take a participant's own white blood cells, add a corrective mRNA instruction, and return the cells to the body. The goal is to temporarily restore the cells' ability to kill germs and see if the procedure is safe and feasible. The study involves 25 men aged 18-75 with a specific CGD mutation.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.