Scientists test mRNA 'Repair' for rare immune disease
NCT ID NCT05189925
Summary
This early-stage study is testing a one-time treatment for Chronic Granulomatous Disease (CGD), a rare genetic disorder where the immune system cannot fight infections properly. Researchers will collect a patient's white blood cells, use messenger RNA (mRNA) to temporarily fix the genetic error in a lab, and then infuse the corrected cells back into the patient. The main goals are to see if this procedure is safe and to find the best dose, with the hope of giving patients's immune cells a temporary boost to fight germs.
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Study contacts
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Contact
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Contact
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Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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