Drug tested to fix faulty protein in cystic fibrosis
NCT ID NCT02325362
Summary
This study tested whether a drug called miglustat could help fix the faulty protein that causes cystic fibrosis in adults with a specific genetic type of the disease. Sixteen participants received either miglustat or a placebo in a crossover design. Researchers measured changes in nasal function and other tests to see if the drug improved the protein's activity.
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Contacts and locations
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Locations
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Assistance publique-Hôpitaux de Paris, Hôpital Cochin
Paris, 75014, France
Conditions
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