New pill hopes to ease rare mitochondrial disease

NCT ID NCT06644534

First seen Jun 26, 2026 · Last updated Jun 26, 2026

Summary

This study tests an oral drug called TTI-0102 in 12 people with MELAS, a rare genetic disorder that causes muscle weakness, strokes, and fatigue. Participants receive either the drug or a placebo for 6 months. Researchers will measure walking ability, fatigue, and quality of life to see if the drug helps control the disease.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

TTI-0102 (cysteamine-pantetheine disulfide)

What this could lead to

If it works, this could point toward a treatment that improves daily function and reduces fatigue for people with MELAS.

What could go wrong

This is a very small early-phase trial with only 12 participants, so results may not apply to everyone. The drug may not show clear benefit or could cause side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

MELAS syndrome

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Angers University Hospital Center (CHU Angers)

    RECRUITING

    Angers, 49100, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Radboud University Medical Center

    RECRUITING

    Nijmegen, 6500 HB, Netherlands

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact