MELAS SYNDROME
Clinical trials for MELAS SYNDROME explained in plain language.
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First-of-its-Kind trial offers hope for devastating genetic disorders
Disease control Recruiting nowThis study is testing a new oral drug called glycerol tributyrate in adults with two rare and serious genetic disorders, MELAS and LHON-Plus. The main goals are to find a safe dose for each person and to see if the drug can improve how their cells produce energy. Each participant…
Matched conditions: MELAS SYNDROME
Phase: PHASE1, PHASE2 • Sponsor: George Washington University • Aim: Disease control
Last updated Mar 27, 2026 12:38 UTC
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New hope for devastating mitochondrial disease
Disease control Recruiting nowThis study is testing whether an oral medicine called TTI-0102 can help control symptoms and improve daily function in people with MELAS, a rare and serious genetic disorder that affects energy production in the body. About 12 participants, aged 16-60 with moderate disease, will …
Matched conditions: MELAS SYNDROME
Phase: PHASE2 • Sponsor: Thiogenesis Therapeutics, Inc. • Aim: Disease control
Last updated Mar 18, 2026 14:41 UTC