Gene therapy injection offers hope for rare childhood blindness

NCT ID NCT07063030

First seen Mar 12, 2026 · Last updated May 02, 2026 · Updated 8 times

Summary

This early-phase study tests a gene therapy called LX107 for people with a rare inherited eye disease that causes vision loss. The treatment is given as an injection under the retina and aims to improve vision and slow disease progression. The study will enroll 13 adults and children aged 4 and older to check if the therapy is safe and shows signs of working.

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Contacts and locations

Locations

  • Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine

    RECRUITING

    Shanghai, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.