Could a daily pill replace growth hormone shots for children?
NCT ID NCT04614337
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests an oral medication called LUM-201 in children with growth hormone deficiency who have not yet received treatment. The goal is to see if taking a pill daily can improve growth as effectively as standard daily injections. The trial also looks for a way to identify which children are most likely to benefit from LUM-201.
What this could mean
Our plain-language read of the trial. This is informational only — not medical advice or a prediction.
Active substance
LUM-201 (oral drug)
What this could lead to
If successful, this could offer a daily pill as an alternative to daily injections for children with growth hormone deficiency.
What could go wrong
This is an early phase 2 trial with a small number of participants, so results may not confirm effectiveness or safety. The drug may not work for all children.
Disclaimer
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This is a summary of
the original study
.
Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Locations
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Atlanta Diabetes Associates
Atlanta, Georgia, 30318, United States
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Canberra Hospital
Garran, Australian Capital Territory, 2605, Australia
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Center of Excellence in Diabetes and Endocrinology
Sacramento, California, 95821, United States
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Children's Hospital of Pittsburgh of UPMC
Pittsburgh, Pennsylvania, 15224, United States
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Children's Minnesota
Saint Paul, Minnesota, 55102, United States
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Children's National Hospital
Washington D.C., District of Columbia, 20010, United States
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Cook Children's Medical Center
Fort Worth, Texas, 76104, United States
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Department of Pediatrics and Endocrinology- Monash Health
Clayton, Victoria, 3168, Australia
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Diabetes & Glandular Disease Clinic, P.A.
San Antonio, Texas, 78229, United States
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Indiana University School of Medicine
Indianapolis, Indiana, 46202, United States
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Klinika Endokrynologii i Chorob Metabolicznych, Instytut Centrum Zdrowia Matki Polki
Lodz, Poland
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Klinika Endokrynologii i Diabetologii Wieku Rozwojowego UM
Wroclaw, Poland
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Klinika Endokrynologii i Diabetologii, Instytut "Pomnik Centrum Zdrowia Dziecka
Warsaw, Poland
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Klinika Pediatrii, Diabetologii i Endokrynologii Gdansk
Pomorskie, Poland
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Klinika Pediatrii, Endokrynologii, Diabetologii z Pododdziałem Kardiologii, Uniwersytecki Dziecięcy Szpital Kliniczny im.Ludwika Zamenhofa w Białymstoku
Bialystok, Poland
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Liggins Institute, University of Auckland
Auckland, New Zealand
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M Health, Fairview Pediatric Specialty Clinics- Discovery Clinic
Minneapolis, Minnesota, 55454, United States
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Medical University of South Carolina
Charleston, South Carolina, 29425, United States
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MultiCare Institute for Research and Innovation
Tacoma, Washington, 98405, United States
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NYU Grossman School of Medicine
New York, New York, 10016, United States
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Nationwide Children's Hospital
Columbus, Ohio, 43205, United States
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Novak Center For Childrens Health
Louisville, Kentucky, 40202, United States
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Pediatric Endocrine Associates
Greenwood Village, Colorado, 80111, United States
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Penn State College of Medicine
Hershey, Pennsylvania, 17033, United States
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Queensland Children's Hospital
South Brisbane, Australia
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Rady Children's Hospital
San Diego, California, 92123, United States
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Royal Children's Hospital
Melbourne, Victoria, 3052, Australia
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SP Dziecięcy Szpital Kliniczny w Warszawie
Warsaw, Poland
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Schneider Children's Medical Center Institute for Endocrinology and Diabetes National Center
Petah Tikva, Tiqwa, 4920235, Israel
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Seattle Children's Hospital
Seattle, Washington, 98105, United States
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Sonomed - Centrum Medyczne
Szczecin, Poland
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State Institution 'V. P. Komissarenko Institute of Endocrinology and Metabolism of the National academy of medical science of Ukraine
Kyiv, 04114, Ukraine
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Texas Tech University Health Sciences Center
Amarillo, Texas, 79106, United States
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The Children's Hospital of Philadelphia
Philadelphia, Pennsylvania, 19104, United States
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The Children's Mercy Hospital
Kansas City, Missouri, 64111, United States
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The Mount Sinai Hospital
Mount Sinai, New York, 30093, United States
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UBMD Pediatrics
Buffalo, New York, 14203, United States
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UMass Memorial Medical Center
Worcester, Massachusetts, 01655, United States
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University of Iowa
Iowa City, Iowa, 52242, United States
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University of Oklahoma Health Sciences Center, Pediatric Diabetes and Endocrinology
Oklahoma City, Oklahoma, 73104, United States
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University of Virginia Health System
Charlottesville, Virginia, 22908, United States
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Wellington Regional Hospital CCDHB
Newtown, Wellington Region, 6021, New Zealand
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klinika Pediatrii, Endokrynologii i Diabetologii Dziecięcej
Rzeszów, Poland