New hope for kids with rare brain tumors: experimental drug enters human testing

NCT ID NCT07158710

First seen Jun 25, 2026 · Last updated Jun 26, 2026 · Updated 2 times

Summary

This early-stage trial tests an oral drug called HSK42360 in children aged 6 to 17 with recurrent malignant brain tumors that have a specific BRAF V600 mutation. The study aims to find the safest dose and check for side effects, while also looking at whether the drug can shrink tumors. About 159 children who have already tried standard treatments without success will take part.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

HSK42360 (oral drug)

What this could lead to

If successful, this could point toward a new treatment option for children with hard-to-treat BRAF-mutant brain tumors.

What could go wrong

This is a very early Phase 1 trial with only 159 participants. The main goal is safety, not proof of effectiveness, and the drug may not shrink tumors or may cause side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

brain cancer

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Department of Neuro-oncology, Cancer Center, Beijing Tiantan Hospital, Capital Medical University,Beijing, China

    RECRUITING

    Beijing, Beijing Municipality, 100070, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Fudan University Affiliated Huashan Hospital

    RECRUITING

    Shanghai, Shanghai Municipality, 200000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The Third Bethune Hospital of Jilin University

    RECRUITING

    Changchun, Jilin, 130000, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • The first affiliated hospital of fujian medical university

    RECRUITING

    Fuzhou, Fujian, 350200, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Xuanwu Hospital Capital Medical University

    RECRUITING

    Beijing, Beijing Municipality, 100021, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Zhujiang Hospital of Southern Medical University

    RECRUITING

    Guangzhou, Guangdong, 510280, China

    Contact Phone: •••-•••-•••• Email: •••••@•••••