First-Ever human test of gene therapy for rare, blinding eye disease begins
NCT ID NCT06467344
Summary
This is the first human trial of an experimental gene therapy called ACDN-01 for people with ABCA4-related eye diseases like Stargardt disease. The study will test the safety and early signs of effectiveness of a single injection into the eye. Fifteen adult participants will be followed for up to five years to see if the treatment can slow or stop vision loss.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Bascom Palmer Eye Institute
RECRUITINGMiami, Florida, 33136, United States
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Casey Eye Institute OHSU
RECRUITINGPortland, Oregon, 97239, United States
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Cincinnati Eye Institute
RECRUITINGCincinnati, Ohio, 45245, United States
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Massachusetts Eye and Ear
RECRUITINGBoston, Massachusetts, 02114, United States
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Retina Consultants of Texas
RECRUITINGHouston, Texas, 77401, United States
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Retina Foundation of the Southwest
RECRUITINGDallas, Texas, 75382, United States
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University of Michigan Kellogg Eye Center
RECRUITINGAnn Arbor, Michigan, 48105, United States
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University of San Francisco
RECRUITINGSan Francisco, California, 94158, United States
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Vitreo Retinal Associates
RECRUITINGGainesville, Florida, 32607, United States
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Wilmer Eye Institute at John Hopkins
RECRUITINGBaltimore, Maryland, 21218, United States
Conditions
Explore the condition pages connected to this study.