STARGARDT DISEASE 1

This is an early safety study testing a new gene therapy called VG801 for people with Stargardt disease, an inherited condition that causes vision loss. The trial will enroll 15 participants, aged 6 and older, who have specific genetic mutations. Doctors will inject the experimen…

This is the first human trial of an experimental gene therapy called ACDN-01 for people with ABCA4-related eye diseases like Stargardt disease. The study will test the safety and early signs of effectiveness of a single injection into the eye. Fifteen adult participants will be f…

This clinical trial is testing whether a medication called tinlarebant can slow the progression of Stargardt disease, a genetic condition that causes vision loss. The study involves 60 participants who will take either the drug or a placebo daily for two years while researchers m…

This study aims to identify people with specific inherited eye diseases, like Stargardt disease, who might be eligible for future treatment trials. It will recruit 50 participants to perform tests that check their genetic profile and eye health. The goal is to create a pool of pr…