Scientists attempt gene fix for rare immune disease

NCT ID NCT00778882

Summary

This early-stage trial aimed to test a gene therapy for males with a rare inherited immune disorder called chronic granulomatous disease (CGD). The approach involved collecting a patient's own blood stem cells, using a modified virus to insert a corrected gene into them, and then returning them to the patient. The goal was to see if this could safely restore the immune system's ability to fight infections, potentially offering a cure.

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Contacts and locations

Locations

  • Seoul National University Hospital

    Seoul, 110-744, South Korea

Conditions

Explore the condition pages connected to this study.