Scientists test 'Base Editing' to fix faulty immune cells
NCT ID NCT06325709
Summary
This study is testing a new gene-editing treatment for adults with a rare, inherited immune disorder called X-linked chronic granulomatous disease (X-CGD). Doctors will collect a patient's own blood stem cells, use a precise gene-editing tool called 'base editing' to try to fix the genetic error, and then return the cells to the patient after chemotherapy. The goal is to see if this one-time treatment can restore proper immune function and reduce severe infections.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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National Institutes of Health Clinical Center
RECRUITINGBethesda, Maryland, 20892, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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