Long-Term study aims to unlock mysteries of rare genetic disorder

NCT ID NCT01905826

First seen Nov 01, 2025 · Last updated May 15, 2026 · Updated 32 times

Summary

This study follows 600 people with GATA2 deficiency, a genetic condition that can affect the immune system and other body systems. Researchers will track participants for up to 15 years to learn why some have mild symptoms while others face serious problems like infections or cancer. The goal is to improve future diagnosis and treatment.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • National Institutes of Health Clinical Center

    RECRUITING

    Bethesda, Maryland, 20892, United States

Conditions

Explore the condition pages connected to this study.