Breakthrough drug trial offers hope for rare muscle disease

NCT ID NCT07038200

Summary

This study is testing an experimental drug called AOC 1020 for people with facioscapulohumeral muscular dystrophy (FSHD), a genetic condition that causes progressive muscle weakness. About 200 participants will receive either the drug or a placebo via IV infusion every six weeks for 78 weeks to see if it improves muscle strength and function. The goal is to control the disease by targeting its underlying genetic cause.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Duke University

    RECRUITING

    Durham, North Carolina, 27708, United States

  • Genge Partners Inc

    NOT_YET_RECRUITING

    Montreal, Quebec, Canada

  • Kansas University Medical Center

    RECRUITING

    Kansas City, Kansas, 66205, United States

  • Kennedy Krieger Institute

    RECRUITING

    Baltimore, Maryland, 21205, United States

  • National Center of Neurology and Psychiatry

    RECRUITING

    Tokyo, Japan

  • National Hospital Organization Osaka Toneyama Medical Center

    RECRUITING

    Osaka, Japan

  • National Hospital Organization Sendai Nishitaga Hospital

    RECRUITING

    Sendai, Japan

  • Ohio State University

    RECRUITING

    Columbus, Ohio, 43221, United States

  • Stanford University

    RECRUITING

    Palo Alto, California, 94304, United States

  • The Ottawa Hospital

    RECRUITING

    Ottawa, Ontario, Canada

  • The University of Osaka Hospital

    RECRUITING

    Osaka, Japan

  • University of Alberta Hospital

    NOT_YET_RECRUITING

    Edmonton, Alberta, Canada

  • University of Calgary - Cumming School of Medicine

    RECRUITING

    Calgary, Alberta, Canada

  • University of California Irvine

    RECRUITING

    Orange, California, 92868, United States

  • University of Colorado

    RECRUITING

    Denver, Colorado, 80045, United States

  • University of Florida

    RECRUITING

    Gainesville, Florida, 32608, United States

  • University of Iowa

    RECRUITING

    Iowa City, Iowa, 52242, United States

  • University of Massachusetts

    RECRUITING

    Worcester, Massachusetts, 01655, United States

  • University of Pennsylvania

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • University of Rochester Medical Center

    RECRUITING

    Rochester, New York, 14642, United States

  • University of Texas Health Science Center at San Antonio

    RECRUITING

    San Antonio, Texas, 78229, United States

  • Virginia Commonwealth University

    RECRUITING

    Richmond, Virginia, 23298, United States

Conditions

Explore the condition pages connected to this study.