New drug aims to stop extra bone formation in rare disease

NCT ID NCT05090891

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This Phase 2 trial tests an experimental drug called INCB000928 (zilurgisertib) in people with fibrodysplasia ossificans progressiva (FOP), a rare genetic condition where soft tissues turn into bone. About 98 participants aged 2 and older will receive either the drug or a placebo daily for several months. The main goal is to see if the drug reduces new abnormal bone growth, which could help control the disease and maintain mobility.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

INCB000928 (zilurgisertib)

What this could lead to

If successful, this drug could slow or prevent the formation of extra bone in people with FOP, potentially reducing disability and improving quality of life.

What could go wrong

This is an early Phase 2 trial with a small number of participants. The drug may not work better than placebo, and side effects are still being studied.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

fibrodysplasia ossificans progressiva myositis ossificans Ossification, Heterotopic

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Albert Einstein Israelite Hospital

    ACTIVE_NOT_RECRUITING

    São Paulo, 05652-900, Brazil

  • Amsterdam Umc - Vu Medisch Centrum (Vumc)

    RECRUITING

    Amsterdam, 1081 HV, Netherlands

  • Ap-Hp Hopital Lariboisiere

    RECRUITING

    Paris, 75010, France

  • Beijing Childrens Hospital Capital Medical University

    RECRUITING

    Beijing, 100045, China

  • Centro de Estudios Reumatologicos

    ACTIVE_NOT_RECRUITING

    Santiago, 7501126, Chile

  • Children'S Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Childrens Hospital of Fudan University

    RECRUITING

    Shanghai, 201102, China

  • Groote Schuur Hospital Radiation Oncology

    ACTIVE_NOT_RECRUITING

    Cape Town, 07925, South Africa

  • Hopital Necker-Enfants Malades

    RECRUITING

    Paris, 75015, France

  • Hospital Italiano de Buenos Aires

    ACTIVE_NOT_RECRUITING

    Buenos Aires, CO 1181, Argentina

  • Hospital Universitario Ramon Y Cajal

    RECRUITING

    Madrid, 28034, Spain

  • Instituto Nacional de Rehabilitacion Luis Guillermo Ibarra

    ACTIVE_NOT_RECRUITING

    Tlalpan, 14389, Mexico

  • Mayo Clinic Rochester

    RECRUITING

    Rochester, Minnesota, 55905, United States

  • Murdoch Children'S Research Institute

    ACTIVE_NOT_RECRUITING

    Parkville, Victoria, 03052, Australia

  • Penn Medicine - Perelman Center For Advanced Medicine

    ACTIVE_NOT_RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

  • Policlinico Universitario Agostino Gemelli Universita Cattolica Del Sacro Cuore

    ACTIVE_NOT_RECRUITING

    Rome, 00168, Italy

  • Royal National Orthopaedic Hospital

    ACTIVE_NOT_RECRUITING

    Stanmore, HA7 4LP, United Kingdom

  • Royal North Shore Hospital

    COMPLETED

    St Leonards, New South Wales, 02065, Australia

  • Seoul National University Hospital

    ACTIVE_NOT_RECRUITING

    Seoul, 03080, South Korea

  • Shanghai Childrens Medical Center

    RECRUITING

    Shanghai, 200127, China

  • Starship Childrens Hospital

    ACTIVE_NOT_RECRUITING

    Auckland, 01023, New Zealand

  • Tongji Hospital of Tongji University

    RECRUITING

    Shanghai, 200065, China

  • Uniklinik Koln

    RECRUITING

    Cologne, 50931, Germany

  • University Health Network Toronto General Hospital

    ACTIVE_NOT_RECRUITING

    Toronto, Ontario, M5G 2N2, Canada