15-Year Check-In: how did early fabry treatment hold up?

NCT ID NCT04002531

First seen Mar 08, 2026 · Last updated May 17, 2026 · Updated 7 times

Summary

This study checked on 5 adults with Fabry disease who had been taking enzyme replacement therapy (ERT) since childhood for about 15 years. Researchers measured kidney function and heart health to see how well the treatment worked over the long term. The goal was to gather information, not to test a new treatment.

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Contacts and locations

Locations

  • Baylor University Medical Center

    Dallas, Texas, 75246, United States

Conditions

Explore the condition pages connected to this study.