New drug tested for Life-Threatening immune storms

NCT ID NCT05001737

Summary

This study tested a drug called emapalumab in children and adults with a dangerous immune system overreaction called Macrophage Activation Syndrome (MAS). MAS can occur in people with Still's disease or lupus who don't respond well to high-dose steroid treatment. The trial aimed to see if emapalumab could control this severe condition and reduce the need for steroids.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Akron Children's Hospital

    Akron, Ohio, 44308, United States

  • Alberta Children's Hospital

    Calgary, Canada

  • Beijing Children's Hospital

    Beijing, China

  • Beijing Friendship Hospital

    Beijing, China

  • Centre Hospitalier Universitaire Sainte-Justine

    Montreal, Canada

  • Centre Hospitalier de l'Université de Montréal

    Montreal, Canada

  • Charité Universitätsmedizin

    Berlin, Germany

  • Children's Healthcare of Atlanta

    Atlanta, Georgia, 30329, United States

  • Children's Hospital of Fudan University

    Shanghai, China

  • Cincinnati Children's Hospital Medical Center

    Cincinnati, Ohio, 45229, United States

  • Fakultní nemocnice Olomouc

    Olomouc, Czechia

  • Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

    Milan, Italy

  • Great Ormond Street Hospital

    London, United Kingdom

  • Hospital Sant Joan de Déu

    Barcelona, Spain

  • Hospital Universitari i Politècnic La Fe

    Valencia, Spain

  • Hospital Universitario

    La Paz, Spain

  • Hospital Universitario La Paz

    La Paz, Spain

  • Hospital for sick children

    Toronto, Canada

  • Hôpital Claude Huriez

    Lille, France

  • Hôpital De La Conception

    Marseille, France

  • Hôpital Necker-Enfants Malades

    Paris, France

  • Hôpital Universitaire Pitié Salpêtrière

    Paris, France

  • IRCCS - Materno-Infantile Burlo Garofolo

    Trieste, Italy

  • IRCCS G. Gaslini

    Genova, Italy

  • Imperial College Healthcare NHS Trust

    London, United Kingdom

  • Nationwide Children's Hospital, Abigail Wexner Research Institute

    Columbus, Ohio, 43205, United States

  • Ortopedyczno - Rehabilitacyjny Szpital Kliniczny im. Wiktora Degi Uniwersytetu Medycznego im. Karola Marcinkowskiego w Poznaniu

    Poznan, Poland

  • Osaka Medical and Pharmaceutical University Hospital

    Takatsuki, Japan

  • Ospedale Pediatrico Bambino Gesù

    Roma, Italy

  • St. Marianna University School of Medicine Hospital

    Kawasaki, Japan

  • Szpital Specjalistyczny im. J. Dietla w Krakowie

    Krakow, Poland

  • Tokyo Medical and Dental University Hospital

    Tokyo, Japan

  • UAB Hospital

    Birmingham, Alabama, 35233, United States

  • UCLA Health

    Los Angeles, California, 90095, United States

  • UMC Utrecht

    Utrecht, Netherlands

  • UPMC Children's Hospital of Pittsburgh

    Pittsburgh, Pennsylvania, 15213, United States

  • Universitair Ziekenhuis Leuven

    Leuven, Belgium

  • University of Calgary

    Calgary, Canada

  • University of Florida

    Gainesville, Florida, 32610, United States

  • University of Minnesota Masonic Children's Hospital

    Minneapolis, Minnesota, 55455, United States

  • Universitätsklinikum Heidelberg

    Heidelberg, Germany

  • Vseobecna Fakultni Nemocnice v Praze

    Prague, Czechia

  • Wojewódzki Specjalistyczny Szpital Dziecięcy im. św. Ludwika w Krakowie

    Krakow, Poland

  • Yokohama City University Hospital

    Yokohama, Japan

Conditions

Explore the condition pages connected to this study.