New hope for rare blood disorder: drug boosts blood cell production

NCT ID NCT03988608

First seen Jan 09, 2026 · Last updated May 15, 2026 · Updated 20 times

Summary

This study tested a drug called eltrombopag in 20 Chinese adults with severe aplastic anemia, a rare condition where the bone marrow stops making enough blood cells. The goal was to see if the drug could improve blood cell counts and reduce the need for transfusions. Participants took the drug daily for up to a year, with doses adjusted based on their platelet levels.

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Contacts and locations

Locations

  • Novartis Investigative Site

    Nanjing, Jiangsu, 210000, China

  • Novartis Investigative Site

    Nanchang, Jiangxi, 330006, China

  • Novartis Investigative Site

    Chengdu, Sichuan, 610041, China

  • Novartis Investigative Site

    Tianjin, 300020, China

  • Novartis Investigative Site

    Tianjin, 300052, China

Conditions

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