First human trial of ELP-02 aims to halt rare nerve disease

NCT ID NCT07447557

First seen Mar 16, 2026 · Last updated May 09, 2026 · Updated 12 times

Summary

This study tests a single injection of a new drug, ELP-02, given into the spine for people aged 3 to 20 with a rare genetic nerve disease called CMT4J. The main goal is to see if the drug is safe and if it can slow or stop muscle damage. Only 8 participants will be enrolled in this early-stage trial.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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