CHARCOT-MARIE-TOOTH DISEASE TYPE 4J
Clinical trials for CHARCOT-MARIE-TOOTH DISEASE TYPE 4J explained in plain language.
Never miss a new study
Get alerted when new CHARCOT-MARIE-TOOTH DISEASE TYPE 4J trials appear
Sign up with your email to follow new studies for CHARCOT-MARIE-TOOTH DISEASE TYPE 4J, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
By submitting, you agree to our Terms of use
-
One-Time gene shot aims to stop rare nerve disease in kids
Disease control Recruiting nowThis early-phase trial tests a single injection of gene therapy (ELP-02) into the spinal fluid of 8 children and young adults with CMT4J, a rare genetic nerve disease that causes muscle weakness. The therapy delivers a working copy of the FIG4 gene to nerve cells, potentially slo…
Matched conditions: CHARCOT-MARIE-TOOTH DISEASE TYPE 4J
Phase: PHASE1, PHASE2 • Sponsor: Elpida Therapeutics SPC • Aim: Disease control
Last updated Jul 10, 2026 00:00 UTC
-
New study aims to unravel nerve mysteries in rare diseases
Knowledge-focused Recruiting nowThis study looks at how nerves work in people with Charcot-Marie-Tooth disease and other nerve disorders like CIDP. Researchers will use special electrical tests and ultrasound to measure nerve and muscle changes. The goal is to better understand these conditions, not to test a n…
Matched conditions: CHARCOT-MARIE-TOOTH DISEASE TYPE 4J
Sponsor: Fondazione I.R.C.C.S. Istituto Neurologico Carlo Besta • Aim: Knowledge-focused
Last updated Jun 27, 2026 11:00 UTC