New drug hope for teens with rare bleeding disorder
NCT ID NCT07194850
First seen Nov 01, 2025 · Last updated May 07, 2026 · Updated 26 times
Summary
This study tests an IV medicine called efgartigimod in teens aged 12 to 18 who have had immune thrombocytopenia (ITP) for over a year. ITP causes low platelet counts, leading to bruising and bleeding. The goal is to find the right dose and see if it safely raises platelet levels. Participants first receive either the drug or a placebo for up to 24 weeks, then everyone gets the drug for up to two more years.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Cardiff and Vale NHS Trust - University Hospital of Wales (UHW)
RECRUITINGCardiff, CF14 4XW, United Kingdom
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Gaslini Children's Hospital
RECRUITINGGenoa, 16147, Italy
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Hospital Infantil Universitario Nino Jesus (HIUNJS)
RECRUITINGMadrid, 28009, Spain
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Hospital Materno-Infantil Universitario Gregorio Maranon
RECRUITINGMadrid, 28009, Spain
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Hospital Sant Joan de Deu Barcelona
RECRUITINGEsplugues de Llobregat, 08950, Spain
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Hospital Universitari Vall d'Hebron
RECRUITINGBarcelona, 08035, Spain
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Institutul Clinic Fundeni
RECRUITINGBucharest, 022328, Romania
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Uniwersytecki Szpital Dzieciecy w Lublinie
RECRUITINGLublin, 20-093, Poland
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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