New hope for kids with rare swelling disorder as drug trial begins
NCT ID NCT07298447
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests a drug called donidalorsen in 20 children aged 2 to 12 with hereditary angioedema (HAE), a condition that causes sudden, painful swelling. The goal is to see if the drug is safe and how it works in young bodies. Researchers will monitor side effects and measure how well it prevents swelling attacks.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Ionis Investigative Site
RECRUITINGSanta Monica, California, 90404, United States
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Ionis Investigative Site
RECRUITINGMiami, Florida, 33136, United States
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Ionis Investigative Site
RECRUITINGSt Louis, Missouri, 63141, United States
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Ionis Investigative Site
RECRUITINGCincinnati, Ohio, 45236, United States
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Ionis Investigative Site
RECRUITINGHershey, Pennsylvania, 17033, United States
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Ionis Investigative Site
RECRUITINGMilan, 20157, Italy
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Ionis Investigative Site
RECRUITINGPadova, 35128, Italy
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Ionis Investigative Site
RECRUITINGSan Donato Milanese, 20097, Italy
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Ionis Investigative Site
RECRUITINGWarsaw, 04-501, Poland
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Ionis Investigative Site
RECRUITINGBarcelona, 08035, Spain