New hope for boys with devastating muscle disease

NCT ID NCT07250737

Summary

This program provides access to an experimental drug called AOC 1044 for people with Duchenne muscular dystrophy who have specific genetic mutations. The treatment aims to help produce a functional version of the dystrophin protein that's missing in this disease. Eligible participants must be at least 6 years old and have the specific genetic mutation that responds to this approach.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Arkansas Children's Hospital

    AVAILABLE

    Little Rock, Arkansas, 72202, United States

  • Gillette Children's

    AVAILABLE

    Saint Paul, Minnesota, 55101, United States

  • Rare Disease Research

    AVAILABLE

    Atlanta, Georgia, 30329, United States

Conditions

Explore the condition pages connected to this study.