New hope for kids with rare cancers: expanded access to DFMO

NCT ID NCT03581240

First seen Feb 22, 2026 · Last updated Jun 17, 2026 · Updated 16 times

Summary

This program offers the drug DFMO to children and young adults (up to age 30) with rare, relapsed tumors like neuroblastoma or medulloblastoma that have specific genetic markers. The goal is to control the disease and provide treatment access when standard options are limited. Participants must meet eligibility criteria, including tumor type and disease status.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Penn State Milton S. Hershey Medical Center and Children's Hospital

    AVAILABLE

    Hershey, Pennsylvania, 17033, United States

    Contact Email: •••••@•••••

    Contact

Conditions

The condition(s) this trial relates to.

atypical teratoid rhabdoid tumor ependymoblastoma medulloblastoma medulloepithelioma neuroblastoma Neuroectodermal Tumors, Primitive Typical Teratoid Rhabdoid Tumor

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.