Gene editing breakthrough: new therapy aims to stop sickle cell pain crises

NCT ID NCT06565026

First seen Feb 14, 2026 · Last updated May 16, 2026 · Updated 7 times

Summary

This early-stage study tests a single injection of CS-101, made from a patient's own gene-edited blood stem cells, for severe sickle cell disease. The goal is to see if it is safe and can reduce or eliminate painful vaso-occlusive crises. The study involves 5 participants aged 12 to 35.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • The First Affiliated Hospital of Guangxi Medical University

    RECRUITING

    Nanning, Guangxi, China

    Contact

    Contact

Conditions

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