New shot targets rare ammonia disorder in early human trial

NCT ID NCT06247670

First seen May 02, 2026 · Last updated May 13, 2026 · Updated 2 times

Summary

This early-stage study tests a new drug called CMP-CPS-001 in healthy adults and women with a genetic condition called OTC deficiency, which makes it hard for the body to remove ammonia. The main goal is to check safety and how the drug moves through the body. Participants receive single or multiple doses as a shot under the skin.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Locations

  • Erasmus MC

    Rotterdam, Netherlands

  • Nucleus Network Brisbane (also known as Q-Pharm Pty Ltd)

    Herston, Queensland, Australia

Conditions

Explore the condition pages connected to this study.