New shot targets rare ammonia disorder in early human trial
Disease control
Ongoing
This early-stage study tests a new drug called CMP-CPS-001 in healthy adults and women with a genetic condition called OTC deficiency, which makes it hard for the body to remove ammonia. The main goal is to check safety and how the drug moves through the body. Participants receiv…
Phase: PHASE1 • Sponsor: CAMP4 Therapeutics Corporation • Aim: Disease control
Last updated May 14, 2026 12:01 UTC