New shot targets rare liver disorder in early human tests
Disease control
Ongoing
This early-stage study tests a new drug called CMP-CPS-001 in healthy adults and women who carry a gene for OTC deficiency, a rare liver condition that can cause dangerous ammonia buildup. The main goal is to check the drug's safety and how the body processes it. Participants rec…
Phase: PHASE1 • Sponsor: CAMP4 Therapeutics Corporation • Aim: Disease control
Last updated Jun 27, 2026 12:23 UTC