New study tracks heart disease in rare genetic disorder

NCT ID NCT06865482

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This study follows 65 people with Friedreich ataxia who also have a thickened heart muscle (cardiomyopathy). Researchers will measure changes in heart structure over time using imaging. The goal is to better understand how heart disease progresses in this condition, which could help design future treatments.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

cardiomyopathy Friedreich ataxia heart disorder

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

    Contact Email: •••••@•••••

  • Campinas State University (UNICAMP)

    RECRUITING

    Campinas, São Paulo, 13083-887, Brazil

    Contact Email: •••••@•••••

  • Centre Hospitalier de Universite de Montreal (CHUM)

    RECRUITING

    Montreal, Quebec, H2X 0C1, Canada

    Contact Email: •••••@•••••

  • Cincinnati Children's Hospital

    RECRUITING

    Cincinnati, Ohio, 45229, United States

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Federico II University

    RECRUITING

    Naples, 80131, Italy

    Contact Email: •••••@•••••

  • Hospital Das Clínicas Da Universidade Federal De Minas Gerais (UFMG)

    RECRUITING

    Belo Horizonte, Minas Gerais, 30130, Brazil

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Hospital Univeritario Puerta de Hierro de Majadahonda

    RECRUITING

    Majadahonda, Madrid, 28222, Spain

    Contact Email: •••••@•••••

  • Hospital Universitário Walter Cantídio - Universidade Federal do Ceará

    RECRUITING

    Fortaleza, Ceará, 60430, Brazil

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Indiana University - Riley Children's Health

    RECRUITING

    Indianapolis, Indiana, 46202, United States

    Contact Email: •••••@•••••

  • Institut de Cardiologie Hopital Pitie Salpetriere

    RECRUITING

    Paris, 75013, France

    Contact Email: •••••@•••••

  • Instituto D'or de Pesquisa e Ensino - Hospital São Rafael

    RECRUITING

    Salvador, Estado de Bahia, 41253-190, Brazil

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Mayo Clinic

    RECRUITING

    Rochester, Minnesota, 55905, United States

    Contact Email: •••••@•••••

  • Motol University Hospital and the Second Faculty of Medicine

    RECRUITING

    Prague, 15006, Czechia

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Oregon Health & Science University

    RECRUITING

    Portland, Oregon, 97239, United States

    Contact Email: •••••@•••••

  • UPC Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto

    RECRUITING

    Ribeirão Preto, São Paulo, 14051, Brazil

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • University Hospital Tübingen

    RECRUITING

    Tübingen, Baden-Wurttemberg, 72076, Germany

    Contact Email: •••••@•••••

  • University of California San Diego

    RECRUITING

    La Jolla, California, 92037, United States

    Contact Email: •••••@•••••

  • University of South Florida

    RECRUITING

    Tampa, Florida, 33612, United States

    Contact Email: •••••@•••••

    Contact Email: •••••@•••••

  • Washington University School of Medicine in St. Louis

    RECRUITING

    St Louis, Missouri, 63110, United States

    Contact Email: •••••@•••••